FDA clears first gene therapy for Sanfilippo A, opening new path for families
FDA approves Fayuvi for Sanfilippo A, the first dedicated treatment, raising questions on access, pricing and long-term monitoring.
FDA approves Fayuvi for Sanfilippo A, the first dedicated treatment, raising questions on access, pricing and long-term monitoring.
The administration has named four acting officials as permanent leaders at the FDA, overseeing drugs, biologics, tobacco and AI modernization.
President Trump praised NASA following the launch of the Nancy Grace Roman Space Telescope, highlighting the mission and his public remarks.
A solar eclipse will be visible in parts of the United States next Wednesday. Experts urge use of certified eye protection and checking official timing for your location.
A major new study provides strong reassurance about the use of acetaminophen (paracetamol) and ibuprofen (Advil) during a baby’s first year. Researchers found no evidence that either common pain reliever increases the risk of eczema or bronchiolitis, a respiratory illness that often affects young children. Earlier studies had raised concerns that acetaminophen (Tylenol) given during…
A person’s posture may subtly affect both emotional state and decision-making, according to new research from McGill University. In a laboratory study, participants who sat upright reported more positive feelings and performed better during a task involving risk and reward than participants who slouched or sat in the control condition. The effects were relatively small…
Researchers have developed a bioengineered chewing gum that may offer a new way to target microbes associated with head and neck cancer. In tests involving oral samples from patients, extracts from the gum sharply reduced one virus and two types of bacteria linked to the disease. The research team was led by Henry Daniell of…
The impending collision – predicted to happen at about 02:35 EDT (06:35 GMT) on Wednesday – is expected to captivate astronomers, both amateur and professional. “It’s something really huge smashing into the Moon. It’s not remotely dangerous, we can just watch the show,” says Dr Matt Bothwell, public astronomer at the University of Cambridge. “It’s…
Arginine is an amino acid that supports many essential functions throughout the body. It helps cells build proteins that carry out a wide range of biological processes. The body produces arginine naturally, and people also obtain it from many protein-rich foods. Abnormally low arginine levels have been linked to several diseases, including colon cancer. Sohail…
Dark matter is usually described as an invisible substance that responds only to gravity. But scientists are now exploring a more complex possibility: dark matter particles may also interact through a hidden force of their own. A new study in the Journal of Cosmology and Astroparticle Physics (JCAP) examined what would happen if dark matter…